Cardiology
FDA advisors to weigh new gene therapy for sickle cell anemia
Patients with sickle cell disease may soon have two new treatments to try.
Oct 30, 2023
0
1
News tagged with bone marrow transplant
Genetics
Hospital's pioneering gene therapy aims to free patients of blood disease. Is a cure at hand?
Born with a deadly blood disease, Clint and Alissa Finlayson's adopted daughters—Ada, nine, and Lily, 12—are the first patients on the West Coast to receive a new gene therapy offered by UCSF Benioff Children's Hospital ...
Oct 28, 2023
0
16
Medical research
Dietary supplement modifies gut microbiome—potential implications for bone marrow transplant patients
Researchers at Baylor College of Medicine and the University of Michigan conducted a phase I pilot study to assess the feasibility of using potato starch as a dietary intervention to modify the gut microbiome in bone marrow ...
Oct 19, 2023
0
72
Diseases, Conditions, Syndromes
Boosting a weak immune system: Scientists find an unusual weapon against common virus
Infections with cytomegalovirus (CMV) are extremely common and often pose no major threat to the vast majority of people. They can however be deadly for people whose immune system is weakened, for example, after bone marrow ...
Oct 17, 2023
0
27
Medical research
Drew Weissman, Nobel-winning mRNA pioneer
Drew Weissman's decades of research into mRNA technology paved the way for COVID-19 vaccines, finally earning a Nobel prize for the physician-scientist.
Oct 2, 2023
0
33
Immunology
Making immunotherapy safe for AML
Acute myeloid leukemia (AML), the second most common leukemia in children, is hard to treat and has a five-year survival rate of just 65 to 70%, according to the American Cancer Society. While immunotherapies like monoclonal ...
Sep 30, 2023
0
21
Health informatics
Brazil's diversity makes country a testing ground for a global stem cell biobank, scientists say
A biobank for all, in which a person from any background could find a bone marrow donor for a stem cell transplant, is a major goal for stem cell science. While repositories of cell lines that could be a match for most patients ...
Sep 28, 2023
0
17
Diseases, Conditions, Syndromes
Sickle cell disease continues to face underfunding and lack of research, say researchers
Since its discovery in 1910, sickle cell disease has been considered a death sentence for those that inherited it. But over the years, dedicated pediatric programs and research initiatives have greatly improved patient care ...
Sep 11, 2023
0
1
Oncology & Cancer
Improving CAR T-cell and monoclonal antibody treatment through epitope editing
In a paper, "Epitope editing enables targeted immunotherapy of acute myeloid leukaemia," published in Nature, researchers at the Department of Pediatric Oncology, Dana-Farber Cancer Institute, Boston, introduce a genetic ...
Neuroscience
PS gene-editing shown to restore neural connections lost in brain disorder
A new study from the University of Minnesota is the first to demonstrate the ability for gene therapy to repair neural connections for those with the rare genetic brain disorder known as Hurler syndrome. The findings suggest ...
Aug 21, 2023
0
82
