Genetics
Newer methods may boost gene therapy's use for more diseases
Jordan Janz knew his gamble on an experimental gene therapy for his rare disease might be paying off when he returned to work and a friend sniffed him.
Jun 2, 2021
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News tagged with experimental gene therapy
Medical research
After gene therapy, hemophilia B patients maintain near-normal levels of clotting factor
Researchers are reporting the highest and most sustained levels to date of the essential blood-clotting factor IX in patients with the inherited bleeding disorder hemophilia B. After receiving a single dose of an experimental ...
Dec 3, 2016
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Medical research
Scientists develop alternative to gene therapy: The technique points to safer, simpler potential HIV treatment
Scientists at The Scripps Research Institute have discovered a surprisingly simple and safe method to disrupt specific genes within cells. The scientists highlighted the medical potential of the new technique by demonstrating ...
Jul 1, 2012
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Genetics
Medical breakthrough: Seattle man is first adult to get new gene therapy for vision
Toby Willis gave up on medical miracles long ago.
Apr 10, 2018
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Alzheimer's disease & dementia
Degenerating neurons respond to gene therapy treatment for Alzheimer's disease
Degenerating neurons in patients with Alzheimer's disease (AD) measurably responded to an experimental gene therapy in which nerve growth factor (NGF) was injected into their brains, report researchers at University of California, ...
Aug 27, 2015
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Immunology
Gene therapy restores immunity in infants with rare immunodeficiency disease
A small clinical trial has shown that gene therapy can safely correct the immune systems of infants newly diagnosed with a rare, life-threatening inherited disorder in which infection-fighting immune cells do not develop ...
Apr 17, 2019
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Genetics
Gene therapies only work for some people – so how do we fix this?
Growing up in Devon in the 1980s, brothers James and Matt (names have been changed) had to be careful with their antics – a cut or bruise could land them in hospital.
Jan 15, 2019
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Other
GMO in sport: Genetically Modified Olympians?
As athletes get ready to smash Olympic records in London, scientists are in a high-stakes race of their own to develop a test that will unmask anyone altering their genes in a desperate quest for gold.
Jul 15, 2012
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Oncology & Cancer
Doctors: Long-lasting cell treatment cured leukemia patients
In 2010, doctors treated Doug Olson's leukemia with an experimental gene therapy that transformed some of his blood cells into cancer killers. More than a decade later, there's no sign of cancer in his body.
Feb 6, 2022
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Medical research
Cell-specific mechanism-based gene therapy approach to treat retinitis pigmentosa
In a paper published in the October 2011 issue of Experimental Biology and Medicine, a team of researchers at Columbia University Medical Center led by Stephen Tsang, MD, Ph.D have achieved temporary functional preservation ...
Sep 30, 2011
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