Oncology & Cancer
Updates: MET targeted therapy for EXON 14 mutations in lung cancer
A new editorial paper titled "Latest updates on MET targeted therapy for EXON 14 mutations in lung cancer" has been published in Oncotarget.
Sep 11, 2023
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News tagged with gene therapies
Oncology & Cancer
New genes and natural toxins offer hope for cancer patients unresponsive to chemotherapy
Scientists from Queen Mary University of London have discovered two new genes that cause head and neck cancer patients to be resistant to chemotherapy, and that silencing either gene can make cancer cells previously unresponsive ...
Sep 4, 2023
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Medical research
Gene-tweaked stem cells offer hope against sickle cell disease
A type of gene therapy that precisely "edits" a key bit of DNA might offer a new way to treat sickle cell disease—a painful inherited condition that largely strikes Black children and adults.
Sep 3, 2023
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Diseases, Conditions, Syndromes
New study shows promising evidence for sickle cell gene therapy
New research published in the New England Journal of Medicine indicates that stem cell gene therapy may offer a promising, curative treatment for the painful, inherited blood disorder sickle cell disease (SCD).
Aug 30, 2023
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Genetics
Ophthalmologists test experimental gene therapy for wet age-related macular degeneration
Ophthalmologists at UC Davis Health used an experimental gene therapy last month to treat a patient with wet age-related macular degeneration, or wet AMD. It was the first time the UC Davis Eye Center had used gene therapy.
Aug 29, 2023
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Diseases, Conditions, Syndromes
Researchers develop new model to find potential treatment for neuromuscular diseases
Researchers from the Centre for Gene Therapy & Regenerative Medicine at King's College London, in collaboration with colleagues from University College London, have developed the first truly scalable human iPSC-neuromuscular ...
Aug 29, 2023
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Genetics
Novel gene therapy significantly reduces hearing loss linked to rare disease in mouse model
An international team led by researchers at UCL and the NIHR Great Ormond Street Hospital Biomedical Research Centre have developed in mice a gene therapy that significantly reduces the hearing loss associated with Norrie ...
Aug 29, 2023
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Diseases, Conditions, Syndromes
Team develops new fly model to find treatments for UBA5 deficiency, a rare epileptic brain disorder
Developmental and epileptic encephalopathy (DEE) refers to a group of neurodevelopmental conditions characterized by developmental delay, cognitive impairment, and seizures in children. In 2016, the first case linking variants ...
Aug 29, 2023
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Genetics
Gene therapy targets the brain vasculature
Researchers have developed an engineered adeno-associated virus (AAV) vector that yields high transduction of brain vascular pericytes and smooth muscle cells. The study describing the characterization of this novel AAV capsid ...
Aug 24, 2023
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Oncology & Cancer
Gene therapy study identifies potential new treatment for liver cancer
Gene therapy that induces the body to create microRNA-22 (miR-22), a naturally occurring molecule, successfully treated mice with hepatocellular carcinoma, the most common form of liver cancer.
Aug 24, 2023
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