Medical research
Researchers detail groundbreaking Angelman syndrome development
Researchers at Texas A&M University have developed the first molecular therapeutic for Angelman syndrome to advance into clinical development.
Mar 23, 2023
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News tagged with gene therapy
Cardiology
Anti-aging gene shown to rewind heart age by ten years
An anti-aging gene discovered in a population of centenarians has been shown to rewind the heart's biological age by 10 years. The breakthrough, published in Cardiovascular Research and led by scientists at the University ...
Jan 23, 2023
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Genetics
Loss of epigenetic information can drive aging, restoration can reverse it
An international study 13 years in the making demonstrates for the first time that degradation in the way DNA is organized and regulated—known as epigenetics—can drive aging in an organism, independently of changes to ...
Jan 12, 2023
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Genetics
Infant gene therapy is a breakthrough for Artemis-SCID patients
Ten young children born without functioning immune systems and lacking the ability to fight infections are on track for healthier lives thanks to a new gene therapy treatment pioneered at UC San Francisco, reports a Dec. ...
Dec 21, 2022
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Medical research
Gene therapy for heart attacks in mice just got more precise
If humans are ever going to be able to regrow damaged tissues the way lizards and fish routinely do, it will require the precise control of gene expression in time and place—otherwise you might end up with random cells ...
Dec 13, 2022
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Oncology & Cancer
Liver cancer study encourages caution with certain gene therapies
Research led by Randal J. Kaufman, Ph.D., has found that misfolded proteins in liver cells contribute to the development of liver cancer, shedding new light on the mysterious origins of one of the world's deadliest diseases. ...
Dec 7, 2022
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Neuroscience
Swelling along brain's axons may be true culprit in Alzheimer's disease
The formation of amyloid plaques in the brain is a hallmark of Alzheimer's disease. But drugs designed to reduce accumulations of these plaques have so far yielded, at best, mixed results in clinical trials.
Dec 1, 2022
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142
Genetics
Gene-delivering viruses reach the brain in step toward gene therapy for neurological diseases
Gene therapies can treat, even potentially cure, certain genetic diseases, but it is challenging to deliver the treatments to the parts of the body where they are needed. Researchers have engineered viruses called adeno-associated ...
Nov 22, 2022
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Genetics
New Alzheimer's genes discovered in world's largest study
Two new genes that raise a person's risk of developing Alzheimer's Disease have been discovered by researchers.
Nov 22, 2022
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302
Genetics
Gene therapy targeting overactive brain cells could treat neurological disorders
A new treatment for neurological and psychiatric diseases, that works by reducing the excitability of overactive brain cells, has been developed by UCL researchers.
Nov 3, 2022
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