Biomedical technology

First nonhuman primate model of Usher syndrome confirmed

Those with Usher Syndrome—the leading hereditary cause for simultaneous deafness and blindness, for which there is no treatment—may have a new reason for hope now that researchers have confirmed the first-ever nonhuman ...

Neuroscience

CRISPR-based strategy restores neurons affected by Rett syndrome

Rett syndrome is a rare, progressive neurodevelopmental disorder that typically affects girls, causing severe intellectual disability, loss of motor skills, and autism-like symptoms, and there is currently no cure. Rett syndrome ...

Medical research

Drug can spur liver regeneration in Alagille syndrome

Research led by Associate Professor Duc Dong, Ph.D., has shown for the first time that the effects of Alagille syndrome, an incurable genetic disorder that affects the liver, could be reversed with a single drug. The study, ...

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