The encouraging results of early stage clinical studies and the tremendous amount of preclinical data demonstrating the feasibility and promise of gene therapy to treat disorders of the central nervous system (CNS) are driving ...
Jul 25, 2016
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Fresh insights into how our cells control muscle development could aid understanding of muscular dystrophy and other inherited diseases.
Jun 2, 2016
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A tiny sliver of a person's DNA—several thousand times smaller than a typical gene—produces a molecule that has crucial influence over whether a person has any control over their muscles, according to a paper published ...
Dec 17, 2015
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This week, scientists gathered in Washington, DC for the International Summit on Human Gene Editing to discuss a technology called CRISPR-CAS9, which can insert, remove and change the DNA of basically any organism. It is ...
Dec 4, 2015
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Researchers at the University of Louisville have discovered a mechanism involved in skeletal muscle repair that may enable clinicians to boost the effectiveness of adult stem cell therapies for diseases such as muscular dystrophy. ...
Nov 30, 2015
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World-leading research from the University of Aberdeen has made a significant breakthrough in understanding a form of childhood motor neuron disease.
Nov 9, 2015
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For the first time, researchers have employed a gene-editing technique involving low-dose irradiation to repair patient cells, according to a study published in the journal Stem Cells Translational Medicine. This method, ...
Jul 22, 2015
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Australian researchers have made a critical discovery about a gene involved in muscular dystrophy that could lead to future therapies for the currently untreatable disease.
Jun 17, 2015
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(AP)—Britain has become the first country in the world to allow the creation of human embryos from the DNA of three people, a technique intended to help mothers avoid passing on genetically degenerative diseases to their ...
Feb 25, 2015
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As British lawmakers vote Tuesday on whether to legalize the creation of babies made from the DNA of three people, here are some questions and answers about the proposed techniques and the controversy surrounding them.
Feb 3, 2015
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