Gene therapy for spinal muscular atrophy might have a high up-front price tag. But by screening and treating infants early, the therapy can save both lives and money in the long term.
Aug 03, 2021
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Scientists and doctors at University College London Great Ormond Street Institute of Child Health (UCL GOS ICH) and Great Ormond Street Hospital (GOSH) have given hope of a gene therapy cure to children with a rare degenerative ...
Jun 30, 2021
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New research has found that men who have the Western world's most common genetic disorder are more likely to develop dementia, compared to those without the faulty genes.
Feb 02, 2021
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Researchers at the Garvan Institute of Medical Research have discovered that three patients with a severe genetic immunodeficiency spontaneously repaired the harmful variants in their DNA and restored normal immune function ...
Feb 01, 2021
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Children with cystic fibrosis who do not have pre-existing severe lung damage have mild or asymptomatic illness when infected with COVID-19, a new study has revealed.
Dec 09, 2020
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In the largest study of the genetics of childhood obesity, researchers have looked at why some children gain weight very easily.
Jun 03, 2020
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Having a faulty gene linked to dementia doubles the risk of developing severe COVID-19, according to a large-scale study.
May 26, 2020
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Scientists at the University of Nottingham have taken a step closer towards developing a treatment for the long-term genetic disorder, myotonic dystrophy.
Apr 29, 2020
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Researchers have found that melanoma cells fight anti-cancer drugs by changing their internal skeleton (cytoskeleton) - opening up a new therapeutic route for combatting skin and other cancers that develop resistance to treatment.
Jan 13, 2020
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The US government and the Bill and Melinda Gates Foundation pledged Wednesday to jointly invest $200 million over the next four years to achieve affordable gene therapy-based cures for sickle cell disease (SCD) and HIV.
Oct 23, 2019
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