Medical research

Gene therapy restores hearing in deaf mice

Using gene therapy, researchers at Boston Children's Hospital and Harvard Medical School have restored hearing in mice with a genetic form of deafness. Their work, published online July 8 by the journal Science Translational ...

Genetics

First patient receives novel gene therapy for GSD

Dr. David Weinstein and his team at UConn Health have administered to a patient the world's first investigational gene therapy for potentially deadly glycogen storage disease (GSD).

Medical research

Technique uses 3-D weaving to grow a living hip replacement

With a goal of treating worn, arthritic hips without extensive surgery to replace them, scientists have programmed stem cells to grow new cartilage on a 3-D template shaped like the ball of a hip joint. What's more, using ...

Genetics

CRISPR enhances gene therapy to fight inherited diseases

Gene therapy has shown promise in treating inherited genetic diseases, but a major issue that has frustrated scientists remains: Replacing a "bad" gene with a healthy one often is a short-lived fix. Typically, the healthy ...

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