Diseases, Conditions, Syndromes

New gene therapy poised to transform care for spinal muscular atrophy

The University of Rochester Medical Center (URMC) has been tapped as one of the first institutions in the U.S. to offer a new gene replacement therapy to treat spinal muscular atrophy (SMA). The new treatment can be delivered ...

Genetics

Roche to buy US gene therapy group Spark for $4.3 bn

Swiss pharmaceuticals giant Roche said Monday it reached a deal worth $4.3 billion (3.7 billion euros) to buy US group Spark Therapeutics, which specialises in the development of gene therapy drugs.

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