Researchers studying a rare genetic disorder that causes severe, progressive neurological problems in childhood have discovered insights into biological mechanisms that drive the disease, along with early clues that an amino ...
Feb 22, 2018
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Researchers have discovered a new technique that overcomes one of the major challenges of stem cell therapy.
Jan 25, 2018
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Glucocorticoids, a class of steroid hormone medications often prescribed to patients with Duchenne muscular dystrophy (DMD), offer long-term benefits for this disease, including longer preservation of muscle strength and ...
Nov 22, 2017
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Macrophages, a type of white blood cell involved in inflammation, readily take up a newly approved medication for Duchenne muscular dystrophy (DMD) and promote its sustained delivery to regenerating muscle fibers long after ...
Oct 16, 2017
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A clinician who treated Charlie Gard, the terminally-ill British baby who died last month, said Saturday his short life became a soap opera fuelled by President Donald Trump and the pope.
Aug 5, 2017
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Charlie Gard, the terminally-ill British baby whose plight drew sympathy from Pope Francis and US President Donald Trump and sparked a debate about medical ethics, died on Friday, his mother said.
Jul 28, 2017
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A five-month legal battle over the fate of a terminally-ill British baby that drew the attention of Pope Francis and US President Donald Trump has also stoked an often angry debate about medical ethics and the courts.
Jul 25, 2017
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A British court on Monday gave the parents of 11-month-old Charlie Gard a chance to present fresh evidence that their terminally ill son should receive experimental treatment.
Jul 10, 2017
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The European Court of Human Rights on Tuesday ordered the British government to keep providing a baby with a rare genetic disease with "appropriate" treatment after a London High Court ruling that he should be allowed to ...
Jun 13, 2017
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Researchers at the National Institutes of Health's National Center for Advancing Translational Sciences (NCATS) and the University of Nevada, Reno School of Medicine (UNR Med) have demonstrated that a drug originally targeted ...
Jun 13, 2017
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