Other

The Chinese dad making medicine to treat his dying son

Two-year-old Haoyang has likely just months to live—but the only medicine that can help his rare genetic condition is not found anywhere in China and closed borders due to the COVID-19 pandemic mean he cannot travel for ...

Surgery

After 24 surgeries, Bangladesh 'tree man' relapses

A year ago Abul Bajandar, a Bangladeshi rickshaw-puller dubbed "tree-man" for the bark-like growths that once covered his body, appeared to have made a full recovery from the rare condition that has afflicted him for a decade.

Genetics

Australian breakthrough in stem cell kidney research

New research led by the Murdoch Children's Research Institute (MCRI), has combined gene editing technology with stem cell kidney regeneration to correct a patient's gene mutation.

Diseases, Conditions, Syndromes

New hope for rare disease drug development

Using combinations of well-known approved drugs has for the first time been shown to be potentially safe in treating a rare disease, according to the results of a clinical trial published in the open access Orphanet Journal ...

Medical research

Alcohol by-product destroys blood stem cells

(Medical Xpress)—Scientists at the Medical Research Council (MRC) Laboratory of Molecular Biology have found that stem cells in the body's 'blood cell factory'—the bone marrow—are extremely sensitive to the main breakdown ...

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