Diseases, Conditions, Syndromes

A new treatment for rare muscular disease

Rare diseases are sometimes the most difficult to treat because of a lack of research and fewer participants to study.

Medical research

Good news for menopausal women taking hops supplements

Hop-based dietary supplements that many women use to ease the night sweats and hot flashes commonly reported during menopause aren't likely to cause drug interactions, new research from Oregon State University's Linus Pauling ...

Diseases, Conditions, Syndromes

Potential therapy for rare neurologic disease

A targeted therapy, currently being studied for treatment of certain cancers including glioblastoma, may also be beneficial in treating other neurologic diseases, a study at the University of Cincinnati shows.

Medical research

New therapy could treat children with Hunter disease

A team at the University of Manchester have developed a novel stem cell gene therapy approach to treat children with a devastating genetic disease. The approach is currently being developed for clinical trial in patients ...

Genetics

Gene therapy used to treat Fabry disease—a world first

A team of Canadian physicians and researchers is believed to be the first in the world to have used gene therapy to treat a patient with Fabry disease, a rare inherited enzyme deficiency that can damage major organs and shorten ...

Medical research

Study identifies potential new avenue for treating pompe disease

Researchers at Duke Health have identified a potential new avenue for treating Pompe disease, a rare condition caused by the build-up of glycogen, a storage form of sugar, in cardiac and skeletal muscle, the liver and other ...

Medical research

First-in-man clinical trial for Hunter syndrome underway

A first-in-man clinical trial, testing a newly developed drug for a rare genetic condition called mucopolysaccharidosis type II (MPS II) or Hunter syndrome, is underway at Emory University.

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