News tagged with gene therapies

Renewed hope for gene therapy in rare disease

Between 30 and 40 million people in Europe suffer from rare diseases—many of them children. As most of these diseases have genetic origins, gene therapy is a major hope for their future cure. Until now, ...

Jul 02, 2014
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Gene correction for a rare disease

Angeles suffers from a severe and rare genetic disease called Acute Intermittent Porphyria (AIP). This means, one of her genes restrains her liver to produce a specific protein needed for the metabolism of ...

Jul 02, 2014
popularity 5 / 5 (1) | comments 0