Medications
Cholesterol jab: Why gene silencing drugs may work better than current treatments
The NHS has very recently approved a new cholesterol-lowering jab which will be offered to 300,000 people over the next three years.
Sep 10, 2021
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News tagged with genetic therapy
Medical economics
New gene therapies may soon treat dozens of rare diseases, but expense may limit availability for many
Zolgensma—which treats spinal muscular atrophy, a rare genetic disease that damages nerve cells, leading to muscle decay—is currently the most expensive drug in the world. A one-time treatment of the life-saving drug ...
Sep 1, 2021
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Cardiology
ESC guidelines on cardiac pacing and cardiac resynchronization therapy launched today
The European Society of Cardiology (ESC) Guidelines on cardiac pacing and cardiac resynchronization therapy (CRT) are published online today in European Heart Journal.
Aug 29, 2021
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Diseases, Conditions, Syndromes
Shared antibodies may push COVID variants: study
Researchers at Vanderbilt University Medical Center have found that people recovering from COVID-19 and those vaccinated against the causative virus, SARS-CoV-2, produce identical clones, or groups, of antibody-producing ...
Aug 13, 2021
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Diseases, Conditions, Syndromes
RNA modification may protect against liver disease
A chemical modification that occurs in some RNA molecules as they carry genetic instructions from DNA to cells' protein-making machinery may offer protection against non-alcoholic fatty liver, a condition that results from ...
Jul 19, 2021
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Genetics
Innovative gene therapy 'reprograms' cells to reverse neurological deficiencies
A novel method of gene therapy is helping children born with a rare genetic disorder called AADC deficiency that causes severe physical and developmental disabilities. The study, led by researchers at The Ohio State University ...
Jul 12, 2021
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Medical research
Genetic factors linked to response to common antiviral medications
St. Jude Children's Research Hospital scientists and collaborators in Sweden and Japan are reporting that the enzyme NUDT15 plays a role in how patients respond to antiviral therapy with the common drugs ganciclovir and acyclovir. ...
Jul 8, 2021
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Medical research
First clinical trial involving in vivo CRISPR human gene editing
A team of researchers from Intellia Therapeutics, Inc. and Regeneron Pharmaceuticals has conducted the first clinical trial involving in vivo CRISPR human gene editing. In their paper published in The New England Journal ...
Arthritis & Rheumatism
Pregnancy outcomes affected by both maternal and paternal inflammatory disease
Karin Hellgren and colleagues examined pregnancy outcomes in relation to disease activity and antirheumatic treatment strategies in women with rheumatoid arthritis (RA). This matched cohort study from Sweden and Denmark explored ...
Jun 18, 2021
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Oncology & Cancer
Predicting resistance to anticancer drugs
Cancer cells can develop resistance to therapy through both genetic and non-genetic mechanisms. But it is unclear how and why one of these routes to resistance prevails. Understanding this 'choice' by the cancer cells may ...
Jun 17, 2021
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