In a landmark study, an international consortium led by researchers at Children's Hospital of Philadelphia (CHOP) published the final results of a key clinical trial of the gene therapy CASGEVY (exagamglogene autotemcel) ...
Apr 25, 2024
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A new study led by Indiana University School of Medicine researchers has found that a brain network condition called "explosive synchronization" could be the cause of extreme pain crises in people with sickle cell disease.
Apr 24, 2024
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A drug approved to treat pulmonary arterial hypertension may be effective at managing hypertension and end-organ damage in patients with sickle cell disease, according to a new study published in Lancet Haematology.
Apr 11, 2024
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Most of the estimated 300,000 babies born every year with sickle cell disease, an inherited red blood cell disorder, live in sub-Saharan Africa in nations where there are few resources to treat them.
Apr 3, 2024
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The U.S. Food and Drug Administration late last year approved two breakthrough gene therapies for sickle cell disease patients. Now a new federal program seeks to make these life-changing treatments available to patients ...
Mar 20, 2024
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Their stories are divided into before and after. First, those long years of pain which flooded every moment—school, relationships, work.
Mar 18, 2024
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Adults with sickle cell disease (SCD) are more likely to report employment loss, and caregivers of children with SCD report more missed days of work, according to a study published online Feb. 29 in Blood Advances.
Mar 14, 2024
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Allergic transfusion reactions (ATRs), a potentially life-threatening side effect of blood transfusions with unclear mechanisms, may be linked to food allergies in pediatric patients as per a recent study by scientists from ...
Mar 13, 2024
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A recent article from a multi-institutional group of researchers provides recommendations for music therapy practice and research among individuals with chronic pain using sickle cell disease as an exemplar condition.
Mar 12, 2024
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UdeM's Stéphanie Forté and co-researchers in Canada and Brazil have shown how people with sickle cell disease or sickle cell trait have a higher chance of dying from COVID-19 than the general population.
Feb 29, 2024
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