Various genetic diseases caused by point mutations have no established therapeutic approaches. Prof. Tsukahara and colleagues (Japan Advanced Institute of Science and Technology) are studying a therapeutic method using artificial ...
Oct 14, 2020
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The potential for treating cystic fibrosis (CF) using mRNA therapies or CRISPR gene editing is possible regardless of the causative mutation. CF clinical trials showing that a genotype-agnostic gene therapy for CF is possible ...
Oct 9, 2020
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When Wei Hsi (Ariel) Yeh was a young undergraduate student, one of her close friends went from normal hearing to complete deafness in the span of one month. He was 29 years old. No one knew why he lost his hearing; doctors ...
Jun 3, 2020
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A month ago, there were countless commentaries on the one-year anniversary of the news that Chinese researcher He Jiankui had created the world's first genome-edited twins.
Jan 6, 2020
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Before the news broke internationally that Chinese scientist He Jiankui had allegedly genetically engineered twin girls, only a few people around the world had known about it. One of those was Penn cardiologist Kiran Musunuru.
Dec 12, 2019
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There's no sugar coating it—diabetes is shaping up to become one of the greatest health challenges in modern times. According to the World Health Organization (WHO), one in eleven individuals suffers from diabetes, and ...
Dec 11, 2019
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A new video showing people casually discussing gene editing and designer babies is making waves because of its source: the government-funded group leading efforts to set standards for the ethically dicey science.
Oct 2, 2019
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What makes healthy cells change and become dysfunctional to the point of causing disease? In addition to a disruption in genes that regulate cells, there is another factor in cell misbehavior that involves metabolism, say ...
Jun 24, 2019
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Six months after a Chinese scientist was widely scorned for helping to make the world's first gene-edited babies, he remains out of public view, and new information suggests that others may be interested in pursuing the same ...
May 29, 2019
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The first reported instance of germline gene editing in humans was bad science as well as bad ethics, according to a commentary publishing April 30 in the open-access journal PLOS Biology by Haoyi Wang of the Institute of ...
Apr 30, 2019
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