Genetics

Brighter possibilities for treating blindness

Advances in preclinical research are now being translated into innovative clinical solutions for blindness, a review published in the 10th Anniversary Series of Science Translational Medicine reports.

Genetics

New data suggests nicotine while pregnant alters genes

The Akay Lab biomedical research team at the University of Houston is reporting in the journal Nature Scientific Reports that a possible cure for addiction may be found by following the pathways of significantly altered dopamine ...

Parkinson's & Movement disorders

Innovative gene therapy trial for Parkinson's disease

A trial for a new gene therapy, known as AXO-Lenti-PD, aimed at improving the supply of dopamine in the brains of people with Parkinson's disease has been launched by researchers at UCL and University College London Hospitals ...

Medical research

New therapy could treat children with Hunter disease

A team at the University of Manchester have developed a novel stem cell gene therapy approach to treat children with a devastating genetic disease. The approach is currently being developed for clinical trial in patients ...

Genetics

Gene therapy used to treat Fabry disease—a world first

A team of Canadian physicians and researchers is believed to be the first in the world to have used gene therapy to treat a patient with Fabry disease, a rare inherited enzyme deficiency that can damage major organs and shorten ...

Genetics

UK experts give green light to 'three-parent babies'

British scientists on Wednesday approved the use of so-called "three-parent baby" fertility treatments, paving the way for the country to become the first in the world to officially introduce the procedures.

Medical research

One-time treatment rescues lethal metabolic liver disease in mice

To treat the liver disorder tyrosinaemia type I, one of the most severe forms of the disease, doctors typically use drug therapy. However the treatment is lifelong and a residual risk of liver cancer persists, which is usually ...

page 2 from 5