Hopes were high a decade ago, when a new class of drugs called BET inhibitors emerged for treating blood cancers and solid tumors. Since then, however, results from numerous clinical trials have painted a much more complex ...
Sep 10, 2024
0
17
Bothnia dystrophy is a form of hereditary blindness, prevalent in the region Västerbotten in Sweden. A new study at Karolinska Institutet published in Nature Communications shows that gene therapy can improve vision in patients ...
Sep 10, 2024
0
2
Acne is the most common dermatological condition worldwide and has been shown to have significant psychological effects on sufferers, especially teenagers.
Sep 10, 2024
0
1
Ronald Rodriguez, MD, Ph.D., professor of medical education and urology at Joe R. and Teresa Lozano Long School of Medicine at The University of Texas Health Science Center at San Antonio (UT Health San Antonio), has discovered ...
Sep 9, 2024
0
30
Researchers from Children's Hospital of Philadelphia (CHOP) have tested a preclinical model for an experimental gene therapy designed to treat multiple sulfatase deficiency (MSD), a disorder that affects the brain, lungs, ...
Sep 9, 2024
0
0
Scientists from Trinity College Dublin have developed a highly promising gene therapy to treat glaucoma, a debilitating eye condition that can lead to complete vision loss, and which affects around 80 million people worldwide. ...
Sep 9, 2024
0
2
As a wave of gene therapies with multimillion-dollar price tags hit the market, many employers are dropping coverage and leaving families in a bind.
Sep 9, 2024
0
0
The vision of people with a rare inherited condition that causes them to lose much of their sight early in childhood was 100 times better after they received gene therapy to address the genetic mutation causing it. Some patients ...
Sep 5, 2024
0
118
Researchers at Weill Cornell Medicine have used artificial intelligence to identify drug targets based on mapping regulatory networks in patient tumors. The study, published in Cell Systems, experimentally identified and ...
Sep 5, 2024
0
32
An article in the journal Human Gene Therapy describes the consensus reached by invited experts who participated in a meeting to evaluate the potential carcinogenicity of gene therapies.
Aug 30, 2024
0
0
