Bluebird Bio Inc.'s gene therapy for a brain-wasting disease received accelerated approval from U.S. regulators, making it the first treatment of its kind for children living with cerebral adrenoleukodystrophy.
Sep 19, 2022
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Two children who received Zolgensma, a gene therapy produced by Swiss drugmaker Novartis to treat spinal muscular atrophy, have died from liver failure, the company said Friday.
Aug 12, 2022
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Found in a patient's blood, circulating tumor cells, or CTCs, have powerful potential to indicate how well a cancer treatment is working and guide treatment decisions. Even so, CTC technologies have not yet been widely implemented ...
Aug 3, 2022
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Radiation therapy is a proven approach to destroying tumors. However, it is possible that it might be able to do even more in the future—namely stimulate the immune system at the same time and so fight cancer even more ...
Apr 20, 2022
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Treating babies with antibiotics in the first week of life is linked with a decrease in healthy bacteria necessary amongst others to digest milk and an increase in antimicrobial resistance, research suggests.
Feb 18, 2022
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Two babies have received the first-ever gene therapy for Tay-Sachs disease after over 14 years of development.
Feb 15, 2022
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Children in Rochester were recently among the first in the nation to receive an experimental treatment for Duchenne muscular dystrophy (DMD). The study is part of an accelerating trend of clinical trials involving gene therapies ...
Feb 10, 2022
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Sonodynamic therapy uses ultrasound in combination with drugs to release harmful reactive oxygen species (ROS) at the site of a tumor. However, the treatment isn't very effective because cancer cells can activate antioxidant ...
Dec 8, 2021
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A new study from Linköping University has shown that the tumor-inhibiting gene TET2 is silenced in a large fraction of cases of acute lymphoblastic leukemia (ALL) in children. The scientists show that the gene can be reactivated ...
Aug 25, 2021
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Researchers have used a genetic engineering strategy to dramatically reduce levels of tau—a key protein that accumulates and becomes tangled in the brain during the development of Alzheimer's disease—in an animal model ...
Mar 19, 2021
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