Medications

First drug approved to treat rare metabolic disorder

(HealthDay)—The U.S. Food and Drug Administration approved the first treatment for the rare genetic disorder primary hyperoxaluria type 1 (PH1), the agency announced Monday.

Medical research

Stem cell-based screen identifies potential new treatments

Vision loss related to aging or inherited genetic disease, such as age-related macular degeneration and retinitis pigmentosa (RP), respectively, is estimated to impact 16 million people worldwide and is often caused by defects ...

Diseases, Conditions, Syndromes

EU plans vaccines as regulator sets approval deadline

European countries were on Tuesday given a clear timeframe for the start of their vaccination programmes after the bloc's medicines regulator said it would decide by December 29 whether to grant emergency approval for the ...

Genetics

The genetics of side-effects

Henk-Jan Guchelaar knows all too well the serious problems that the side-effects of medication can cause. As a professor of clinical pharmacy at the University of Leiden in the Netherlands, he has spent the last two decades ...

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