Duchenne muscular dystrophy (DMD) is a a rare and fatal genetically-inherited degenerative neuromuscular disease that affects one in 5,000 newborn boys. While incurable, researchers are searching for therapies that might ...
Feb 1, 2018
0
1
A team of researchers from the U.S. and Germany describes a novel CRISPR approach to produce healthy heart muscle using pluripotent stem cells from Duchenne muscular dystrophy (DMD) patients. In their paper published on the ...
Scientists at Royal Holloway, University of London, along with colleagues at UCL, have developed a novel artificial human chromosome which could be used to reverse the genetic defect in muscle stem cells from patients with ...
Jan 25, 2018
0
26
A new 'checkpoint' model which can be used to identify potential treatments for genetic disorders such as cystic fibrosis and Duchenne muscular dystrophy (DMD) has been proposed by a team of Bradford scientists.
Dec 18, 2017
0
3
Regenerative medicine researchers at UT Southwestern Medical Center developed an improved and simplified gene-editing technique using CRISPR/Cas9 tools to correct a common mutation that causes Duchenne muscular dystrophy.
Nov 30, 2017
0
195
Glucocorticoids, a class of steroid hormone medications often prescribed to patients with Duchenne muscular dystrophy (DMD), offer long-term benefits for this disease, including longer preservation of muscle strength and ...
Nov 22, 2017
0
0
After boys and young men with Duchenne muscular dystrophy received cardiac progenitor cell infusions, medical tests indicated that the patients' hearts appeared improved, results from a new study show. Patients in the study ...
Nov 15, 2017
0
1
This time of year, doctors often recommend flu shots for people who are young, old, pregnant or immunocompromised.
Oct 26, 2017
0
126
The U.S. Food and Drug Administration has rejected an experimental drug for a common type of muscular dystrophy.
Oct 25, 2017
0
1
Critical Path Institute (C-Path) and The Clinical Data Interchange Standards Consortium (CDISC) announce the open availability of a Duchenne Muscular Dystrophy Therapeutic Area User Guide ( TAUG-DMD v1.0), which describes ...
Oct 18, 2017
0
1
