Genetics
US scientists try first gene editing in the body
Scientists for the first time have tried editing a gene inside the body in a bold attempt to permanently change a person's DNA to try to cure a disease.
Nov 15, 2017
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Page 2 - News tagged with gene therapies
Alzheimer's disease & dementia
Study shows how exercise generates new neurons, improves cognition in Alzheimer's mouse
A study by a Massachusetts General Hospital (MGH) research team finds that neurogenesis -inducing the production of new neurons—in the brain structure in which memories are encoded can improve cognitive function in a mouse ...
Sep 6, 2018
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Genetics
Man blind for 40 years regains some sight through gene therapy
Doctors for the first time have used a form of gene therapy to restore partial vision in a blind person, according to findings announced Monday.
May 24, 2021
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Diseases, Conditions, Syndromes
A family's history with cystic fibrosis
Wanda (Lemna) O'Neal was four years old when her sister Nancy died.
Apr 24, 2015
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Medical research
Subset of stem cells identified as source for all cells in blood and immune systems
Researchers at Fred Hutchinson Cancer Research Center have identified a specific subset of adult blood stem cells that is exclusively responsible for repopulating the entire blood and immune system after a transplant.
Nov 1, 2017
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Medical research
Gene therapy for Duchenne muscular dystrophy safely preserves muscle function
A gene therapy being developed at Penn Medicine to treat Duchenne muscular dystrophy (DMD) successfully and safely stopped the severe muscle deterioration associated with the rare, genetic disease in both small and large ...
Oct 7, 2019
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Diseases, Conditions, Syndromes
Collaboration develop a potent therapy candidate for fatal prion diseases
Drug development is typically slow: the pipeline from basic research discoveries that provide the basis for a new drug to clinical trials to production of a widely available medicine can take decades. But decades can feel ...
Jun 27, 2024
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Genetics
Gene therapy breakthrough in treating rare form of blindness
Positive results of the world's first gene therapy trial for a genetic cause of blindness known as choroideremia have been reported in Nature Medicine.
Oct 9, 2018
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Genetics
Regeneration across complete spinal cord injuries reverses paralysis
When the spinal cords of mice and humans are partially damaged, the initial paralysis is followed by the extensive, spontaneous recovery of motor function. However, after a complete spinal cord injury, this natural repair ...
Sep 21, 2023
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Immunology
Gene therapy could 'turn off' severe allergies
A single treatment giving life-long protection from severe allergies such as asthma could be made possible by immunology research at The University of Queensland.
Jun 2, 2017
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