Cancer is a complex disease and only thanks to advances in genomic techniques have researchers begun to understand, at a cellular and molecular level, the mechanisms which are disrupted in cancer cells. This knowledge is ...
Nov 22, 2012
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An improved gene therapy treatment can cure mice with cystic fibrosis (CF). Cell cultures from CF patients, too, respond well to the treatment. Those are the encouraging results of a study presented by the Laboratory for ...
Nov 16, 2015
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A girl saw her mother's face for the first time. A boy tore through the aisles of Target, marveling at toys he never knew existed. A teen walked onto a stage and watched the stunned expressions of celebrity judges as he wowed ...
Oct 9, 2017
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Two babies have received the first-ever gene therapy for Tay-Sachs disease after over 14 years of development.
Feb 15, 2022
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Found in a patient's blood, circulating tumor cells, or CTCs, have powerful potential to indicate how well a cancer treatment is working and guide treatment decisions. Even so, CTC technologies have not yet been widely implemented ...
Aug 3, 2022
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Researchers at Moffitt Cancer Center have found that a deficiency in an important anti-tumor protein, p53, can slow or delay DNA repair after radiation treatment. They suggest that this is because p53 regulates the expression ...
Apr 23, 2013
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Could humanity finally be gaining the upper hand in our age-old fight against cancer?
Feb 2, 2023
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Final 12-month data from the EXACT trial demonstrates safety and efficacy results for a vascular endothelial growth factor (VEGF) gene therapy treatment for patients who have advanced coronary artery disease (CAD). The late-breaking ...
May 2, 2024
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People with one form of the genetic blood disorder hemophilia now have a one-time treatment with a $3.5 million price tag.
Nov 23, 2022
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Children in Rochester were recently among the first in the nation to receive an experimental treatment for Duchenne muscular dystrophy (DMD). The study is part of an accelerating trend of clinical trials involving gene therapies ...
Feb 10, 2022
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