Oncology & Cancer
An ancient anti-cancer mechanism: DISE
A new editorial paper titled "DISE, an ancient anti-cancer mechanism that senses mutational load in cancerous cells?" has been published in Oncotarget.
Oct 3, 2023
0
1
Page 5 - News tagged with gene therapy treatment
Cardiology
New scanning methods can detect deadly heart condition before symptoms appear
Combining two types of heart scan techniques could help doctors to detect the deadly heart condition hypertrophic cardiomyopathy (HCM) before symptoms and signs on conventional tests appear, according to a new study led by ...
Jul 19, 2023
0
51
Medications
FDA approves first gene therapy for severe hemophilia A
The U.S. Food and Drug Administration on Thursday approved a costly single-dose gene therapy for patients with severe hemophilia A, a life-threatening hereditary bleeding disorder.
Jul 3, 2023
0
1
Genetics
FDA approves first gene therapy to treat Duchenne muscular dystrophy
The U.S. Food and Drug Administration on Thursday approved the drug Elevidys (delandistrogene moxeparvovec-rokl), the first gene therapy for the treatment of children with Duchenne muscular dystrophy (DMD).
Jun 26, 2023
0
1
Diseases, Conditions, Syndromes
Treatment cost analysis highlights systemic health inequities faced by persons with sickle cell disease
A new distributional cost-effectiveness analysis of gene therapy versus standard-of-care for sickle cell disease (SCD) found that while gene therapy is cost-ineffective by conventional measures, it can be an equitable therapeutic ...
May 29, 2023
0
4
Medications
FDA-approved drug shows promise in lab models for childhood blinding disease
A National Institutes of Health team has identified a compound already approved by the U.S. Food and Drug Administration that keeps light-sensitive photoreceptors alive in three models of Leber congenital amaurosis type 10 ...
Mar 29, 2023
0
7
Oncology & Cancer
From vaccines to AI: New weapons in the fight against cancer
Could humanity finally be gaining the upper hand in our age-old fight against cancer?
Feb 2, 2023
0
22
Medications
FDA approves gene therapy for tough-to-treat bladder cancer
Patients with a high-risk bladder cancer now have a new option to treat it.
Dec 19, 2022
0
4
Medications
A gene therapy for hemophilia that costs $3.5 million gets FDA approval
People with one form of the genetic blood disorder hemophilia now have a one-time treatment with a $3.5 million price tag.
Nov 23, 2022
0
13
Oncology & Cancer
New cancer therapy takes personalized medicine to a new level
Personalized care has been a buzzword in medicine for years, but new research on cancer treatment is taking it to a new level.
Nov 13, 2022
0
33
