Neuroscience

Economic, fast and efficient cell-type targeting

It is a remarkable proof for the concept of IOB: working closely hand in hand, our molecular and clinical researchers have developed a library of 230 adeno associated viral vectors (AAVs), each with a different synthetic ...

Neuroscience

Retina restructures itself after cell death

Following gene therapy, the retina can restructure itself and regain normal light responses, according to research in mice published in JNeurosci. These results emphasize the plasticity of the retina and support ongoing development ...

Oncology & Cancer

Genetically modified virus combats prostate cancer

Researchers at the São Paulo State Cancer Institute (ICESP) in Brazil have used a genetically manipulated virus to destroy tumor cells upon injection into mice with prostate cancer. The virus also made tumor cells more sensitive ...

Medical research

The role of family doctors in advanced therapies

A recent study conducted jointly by the Tissue Engineering Research Group of the Department of Histology and the family medicine Unit of the University of Granada (UGR) has highlighted the conceptual, attitudinal and procedural ...

Diseases, Conditions, Syndromes

New gene therapy poised to transform care for spinal muscular atrophy

The University of Rochester Medical Center (URMC) has been tapped as one of the first institutions in the U.S. to offer a new gene replacement therapy to treat spinal muscular atrophy (SMA). The new treatment can be delivered ...

Genetics

Brighter possibilities for treating blindness

Advances in preclinical research are now being translated into innovative clinical solutions for blindness, a review published in the 10th Anniversary Series of Science Translational Medicine reports.

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Gene therapy

Gene therapy is the insertion of genes into an individual's cells and tissues to treat a disease, such as a hereditary disease in which a deleterious mutant allele is replaced with a functional one. Although the technology is still in its infancy, it has been used with some success. Antisense therapy is not strictly a form of gene therapy, but is a genetically-mediated therapy and is often considered together with other methods.

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