Diseases, Conditions, Syndromes

FDA clears investigational drug for ALS gene therapy trials

Apic Bio, a gene therapy company developing treatment options for patients with rare genetic diseases and co-founded by UMass Medical School's Robert H. Brown Jr., DPhil, MD, announced that the FDA has cleared its investigational ...

Medical research

Structure of enzyme seen as target for ALS drugs

Investigators from the School of Medicine at The University of Texas Health Science Center at San Antonio have determined the first high-resolution structure of an enzyme that, if partially inhibited, could represent a new ...

Genetics

Researchers discover new type of CRISPR gene scissors

Like humans, bacteria and archaea can be attacked by viruses. These microorganisms have developed their own immune defense strategies against their pathogens. Bacterial defenses, such as CRISPR-Cas systems, have diverse proteins ...

Medications

Testing remdesivir as a potential treatment for COVID-19

Rush University Medical Center is participating in a new clinical trial to test the effectiveness of the drug remdesivir in the treatment of coronavirus disease 2019 (COVID-19). This disease currently has no approved treatment.

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