As a new generation of gene therapy clinical trials shows promise to cure or halt the progression of several rare diseases, the time has come to explore ways to pay for the cutting edge treatments, a pediatric hematologist-oncologist ...
May 26, 2016
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Monthly blood transfusions can substantially reduce the risk of recurrent strokes in children with sickle cell disease (SCD) who have already suffered a silent stroke, according to the results of an international study by ...
Aug 20, 2014
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A recent study from researchers at University Hospitals (UH) Connor Whole Health has examined variables associated with engagement in integrative health and medicine (IHM) and nonpharmacologic modalities rather than opioids ...
Jan 23, 2024
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Sickle cell anaemia is most common in Africa and up to 11,000 children are born with the condition every year in Tanzania alone. Yet most of what is known about the genetic basis of this inherited disease comes from studies ...
Nov 6, 2014
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A new gene therapy for sickle cell disease has been deemed safe by a U.S. Food and Drug Administration advisory panel, paving the way for full approval by early December 2023.
Nov 2, 2023
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In a study published today in Blood Advances, researchers found that privately insured individuals with sickle cell disease (SCD) spend approximately $1.7 million on disease-related medical expenses over their lifetime. These ...
May 16, 2022
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The presence of sickle cell trait among African Americans may help explain why those on dialysis require higher doses of an anemia medication than patients of other ethnicities, according to a study appearing in an upcoming ...
Jan 23, 2014
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Sickle cell disease refers to a group of inherited blood disorders with symptoms like anemia and blocked blood vessels. About 80% of the world's sickle cell disease cases occur in sub-Saharan Africa. Lack of access to comprehensive ...
Aug 8, 2023
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A national sickle cell disease study involving Medical University of South Carolina researchers found that for some children with sickle cell disease, the drug hydroxyurea is as effective as blood transfusions to reduce blood ...
Jan 4, 2016
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Swiss-based pharmaceuticals giant Novartis said Monday it was acquiring Selexys Pharmaceuticals Corp., a US research lab in blood and inflammatory disorders, in a deal costing up to $665 million (627 million euros).
Nov 21, 2016
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