Disease or Syndrome: Spinal Muscular Atrophy

Medical news and research articles

Wearable knee robot could help children with muscle weakness

A lightweight robotic device that facilitates neuromuscular recovery in children with spinal muscular atrophy (SMA), helping them to stand unassisted, is published in Nature this week. Improved function persists after discontinuing ...

Short-circuiting pancreatic cancer: A potential RNA therapy

Pancreatic ductal adenocarcinoma (PDAC) is the most lethal form of pancreas cancer. It's also the most common form of the disease. Potential treatments typically target a key mutated oncogene called KRAS. In some cases, PDAC ...

FDA approves Itvisma for spinal muscular atrophy

The U.S. Food and Drug Administration has approved Itvisma (onasemnogene abeparvovec-brve) for the treatment of spinal muscular atrophy (SMA) in patients 2 years and older with confirmed mutation in the survival motor neuron ...

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