Q&A: Gene editing is coming for common diseases. Cardiologists discuss if we are ready
Gene therapy is no longer the future of medicine—it's reality. Treatments that replace, silence or edit genes are already changing clinical care.
Oct 20, 2026
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Therapeutic or Preventive Procedure: Gene Therapy
Medical news and research articles
Gene editing approach opens potential new route to Alzheimer's treatment
Dr. Kevin Kemp and his research team at the University of Bristol have converted the high-risk Alzheimer's gene APOE4 into the lower-risk APOE3 gene.
Sep 29, 2026
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From autism to Alzheimer's: Membrane transporters open new avenues for treating brain disorders
Solute carriers (SLCs) are specialized transport proteins that control the movement of nutrients, ions and neurotransmitters across cell membranes and are essential for brain metabolism and neuronal communication. While some ...
Sep 10, 2026
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Blocking a microRNA reverses deadly lung disease in multiple models
Researchers blocked a naturally occurring molecule to reverse pulmonary arterial hypertension in preclinical models, a finding that could point to a new treatment approach for people with a rare and often fatal lung disease.
Sep 2, 2026
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Restoring inhibitory neuron plasticity may reverse neurodevelopmental disorder symptoms, preclinical study suggests
Some of the symptoms of neurodevelopmental disorders (NDDs), such as autism spectrum disorder and epilepsy, may result from dysfunction of certain neurons in the brain and their ability to change their properties in response ...
Aug 12, 2026
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Death of girl in Chinese gene-editing trial kept secret: Report
A 6-year-old Chinese girl died last year after receiving an experimental gene therapy to correct a non-life-threatening condition, according to an investigation by Science and Retraction Watch.
Jul 24, 2026
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Premature blood stem cell aging in sickle cell disease may be reversible
Sickle cell disease causes premature aging of blood stem cells, which scientists may be able to address with a special class of drugs, according to a new study from St. Jude Children's Research Hospital. Patients with sickle ...
Jul 23, 2026
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FDA drug approval affects health care around the world, but political shortcuts could hurt the agency's reputation
At the beginning of July 2026, the U.S. Food and Drug Administration approved the first gene therapy for young children with sickle cell disease.
Jul 15, 2026
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Gene therapy restores key fragile X traits in preclinical study
A gene therapy designed to replace the missing protein that causes fragile X syndrome restored several disease-relevant traits in a mouse model, according to a new study published in Gene Therapy.
Jul 15, 2026
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How 'peacemakers' of the immune system could unlock long-term disease remission
"Peacemaker" immune cells could help treat diseases ranging from type 1 diabetes to neurodegeneration by restoring immune tolerance, according to a new paper in Frontiers in Science.
Jun 25, 2026
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