Doctors seek best way to treat newly discovered genetic disorder
Most folks probably think of gene mutations as something people are born with, but genes can also change later in life, sometimes making people sick.
Aug 18, 2025
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Therapeutic or Preventive Procedure: Hematopoietic Stem Cell Transplantation
Medical news and research articles
Replacing brain immune cells in mice slows neurodegeneration: Technique may help with diseases like Alzheimer's
Tay-Sachs and Sandhoff diseases, genetic disorders affecting the brain, have no effective treatment and are typically fatal within the first years of life.
Aug 6, 2025
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Beta-HPV can directly cause skin cancer in immunocompromised people, research reveals
Researchers at the National Institutes of Health (NIH) have shown for the first time that a type of human papillomavirus (HPV) commonly found on the skin can directly cause a form of skin cancer called cutaneous squamous ...
Jul 30, 2025
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New drug combination effective for T-cell lymphoma patients
Relapsed/refractory peripheral and cutaneous T-cell lymphomas (R/R PTCL and CTCL) are aggressive blood cancers that often resist standard therapy. Patients with these lymphomas may require stem cell transplants, but the disease ...
Jul 1, 2025
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We have drugs to manage HIV. So why are we spending millions looking for cures?
Over the past three decades, there have been amazing advances in treating and preventing HIV.
Jul 1, 2025
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New development in stem cell transplant for blood cancers set to change 40 years of standard practice
Australian researchers have demonstrated that the use of a new, less toxic drug combination after stem cell transplants for leukemia significantly improves patient outcomes post-transplant, reducing the risk of the life-threatening ...
Jun 16, 2025
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Oral drug shows promise for slowing fatal childhood brain disease
A Kennedy Krieger Institute researcher is playing a role in a major international effort that has yielded a promising first-ever drug treatment for cerebral adrenoleukodystrophy (cALD)—a rare, often fatal genetic brain disease ...
Jun 2, 2025
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Stem cell transplant offers potentially curative therapy in pediatric patients with monogenic inflammatory bowel disease
A collaborative team of researchers from Children's Hospital of Philadelphia (CHOP) found that hematopoietic stem cell transplantation (HSCT) is a highly effective method for treating patients with monogenic inflammatory ...
May 21, 2025
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Investigational gene therapy gives children with rare immune disorder a new lease on life
An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life-threatening immune disorder called severe leukocyte adhesion deficiency-I, or LAD-I, in an international ...
Apr 30, 2025
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How stem cells calm the body's immune response
Our blood consists of many cell types that develop through different stages from a precursor type—the blood stem cell. An international research team led by Universitätsmedizin Frankfurt and Goethe University has now investigated ...
Mar 21, 2025
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