MeSH tree: C16.320.322
Research using human brain organoids onboard the International Space Station helped lead to a clinical trial of a potential therapy for Rett syndrome, a debilitating neurological disorder in children. Scientists are now expanding ...
Aug 19, 2026
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I teach a university course called Hormones and Behaviour. What surprises students is that biological sex is not produced by a single switch. What surprises me is that many students have never been taught this before. It ...
Aug 14, 2026
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A protein best known for protecting the ends of chromosomes also helps muscle stem cells preserve their identity and repair damaged tissue, according to a new study from researchers at the Perelman School of Medicine at the ...
Jul 31, 2026
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In a study published in the journal Science, researchers in Queensland and the United States discovered that the human X chromosome attracts an unusual kind of DNA mutation, potentially doubling the risk of certain genetic ...
Jul 31, 2026
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A cell therapy called deramiocel could slow muscle weakening in boys and young men with advanced Duchenne muscular dystrophy (DMD) and may also slow heart damage in those who already have heart muscle disease, a Phase III ...
Jul 29, 2026
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Researchers at the USF Health Morsani College of Medicine have identified a potential pathway that could protect cardiac function in people with Duchenne muscular dystrophy (DMD), a progressive and fatal genetic disease that ...
Jul 17, 2026
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A gene therapy designed to replace the missing protein that causes fragile X syndrome restored several disease-relevant traits in a mouse model, according to a new study published in Gene Therapy.
Jul 15, 2026
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How are disease-relevant molecules distributed within tissue? What changes occur even before they become visible under the microscope? Questions such as these are crucial for early diagnosis and targeted treatment in many ...
Jul 13, 2026
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At Binghamton University, researchers were among the first to find ways to help patients with Duchenne muscular dystrophy (DMD) through the development of an effective drug. Now, they are continuing that work, looking to ...
Jun 30, 2026
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A gene therapy designed to replace a missing brain protein restored normal brain activity and improved behavior in a mouse model of fragile X syndrome (FXS), according to a study led by researchers at the University of California, ...
Jun 20, 2026
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