Congenital, Hereditary, and Neonatal Diseases and Abnormalities: News and Research on Argininosuccinic Aciduria

mRNA technology could be possible treatment for rare liver genetic disease

By exploiting the technology used in COVID-19 vaccines, a team led by UCL, King's College London and Moderna scientists has created an effective therapy for a rare disease, in a study in mice, demonstrating the technology's ...