Hemic and Lymphatic Diseases: News and Research on Hemorrhagic Disorders

MeSH tree: C15.378.463

FDA approves Waskyra for Wiskott-Aldrich syndrome

The U.S. Food and Drug Administration has approved Waskyra (etuvetidigene autotemcel) as the first cell-based gene therapy for the treatment of Wiskott-Aldrich syndrome (WAS).

page 4 from 29