MeSH tree: C10.668.491.175
Duchenne muscular dystrophy (DMD) is a muscle degeneration disorder caused by mutations affecting the dystrophin gene. On August 24 in the journal Stem Cell Reports, researchers show how a dual CRISPR RNA method restored ...
Aug 24, 2023
0
164
Duchenne muscular dystrophy (DMD) is a common progressive muscular disorder. It is an X-chromosome-linked disorder that gradually weakens various muscle groups including those supporting the heart, thus resulting into early ...
Aug 17, 2023
0
60
A new method allows large quantities of muscle stem cells to be safely obtained in cell culture. This provides a potential for treating patients with muscle diseases—and for those who would like to eat meat, but don't want ...
Aug 16, 2023
0
85
New research by the Pragmatic Health Ethics Research Unit of the Montreal Clinical Research Institute (IRCM), affiliated with University of Montreal, highlights the colossal challenges faced by people living with one or more ...
Aug 8, 2023
0
42
Nine people around the world who have been living with unexplained, muscular dystrophy-like symptoms may now have an answer for what is causing the progressive muscle weakness in their body's mid-section, arms and legs.
Jul 17, 2023
0
71
A group of Ludwig Maximilian University scientists led by Eckhard Wolf has developed a porcine DMD model with a mutation that mimics the hallmarks of the human disease but develops them in an accelerated mode. The study is ...
Jul 13, 2023
0
45
The U.S. Food and Drug Administration on Thursday approved the drug Elevidys (delandistrogene moxeparvovec-rokl), the first gene therapy for the treatment of children with Duchenne muscular dystrophy (DMD).
Jun 26, 2023
0
36
It's not easy to distinguish between the dozens of subtypes of limb girdle muscular dystrophy—a rare, genetic muscle disease characterized by weakness in the hips and shoulders that causes difficulty walking and lifting the ...
Jun 15, 2023
0
58
The lone volunteer in a gene-editing study targeting a rare form of Duchenne muscular dystrophy likely died after having a reaction to the virus that delivered the therapy in his body, researchers concluded in an early study.
Jun 1, 2023
0
103
A team of researchers at the University of Houston College of Pharmacy is reporting that by manipulating TAK1, a signaling protein that plays an important role in development of the immune system, they can slow down disease ...
May 24, 2023
0
45
