Researchers are closer to finding a better way to treat children with a rare metabolic disorder called MPS I. It is caused by a deficiency of the key enzyme IDUA needed to break down complex sugars in cells. MPS I eventually ...
Jul 28, 2016
0
370
With a goal of treating worn, arthritic hips without extensive surgery to replace them, scientists have programmed stem cells to grow new cartilage on a 3-D template shaped like the ball of a hip joint. What's more, using ...
Jul 18, 2016
0
285
Northwestern Medicine scientists have shown how manipulating a novel target in the brain using gene therapy could lead to new treatments for depression.
Jul 12, 2016
0
96
Adolescents and young adults with a severe inherited immunodeficiency disorder improved following treatment with novel gene therapy developed at St. Jude Children's Research Hospital and at the National Institute of Allergy ...
Apr 20, 2016
0
81
For the first time, scientists have confirmed the long-standing hypothesis that as people age, they accumulate gene mutations in their mitochondria—cells' energy source.
Apr 14, 2016
1
83
Gene therapy, whereby a patient's disorder is treated by inserting a new gene, replacing a defective one, or disabling a harmful one, suffered a setback in 1999, when Jesse Gelsinger, an 18-year-old with a genetic liver disease, ...
Jan 28, 2016
1
79
Research from Boston Children's Hospital suggests the possibility of restoring at least some visual function in people blinded by optic nerve damage from glaucoma, estimated to affect more than 4 million Americans, or from ...
Jan 14, 2016
0
1089
Scientists have uncovered part of a protein found in humans and other primates that can help us fight off HIV. In a new study published in the journal Heliyon, researchers discover how this structure can stop HIV from working ...
Jan 14, 2016
0
123
Results from a long-term clinical trial conducted by cancer researchers at Houston Methodist Hospital show that combining radiation treatment with "suicide gene therapy," a technique in which prostate cancer cells are genetically ...
Dec 12, 2015
0
467
Twenty years ago, scientists discovered that short strands of RNA known as microRNA help cells to fine-tune their gene expression. Disruption or loss of some microRNAs has been linked to cancer, raising the possibility of ...
Dec 7, 2015
1
71
