Congenital, Hereditary, and Neonatal Diseases and Abnormalities: News and Research on Anemia, Hemolytic, Congenital

MeSH tree: C16.320.070

Custom alterations: Mending genes for long-lasting effects

Gene-editing therapies—techniques that modify DNA to treat or prevent disease—have the potential to transform the field of drug development. By making precise edits to the genome, problematic genes could be modified or eliminated, ...

Q&A: Shedding light on a neglected form of sickle cell disease

Sickle cell disease (SCD) is a group of painful and life-threatening genetic disorders that affect hemoglobin, the major protein that carries oxygen in red blood cells. It occurs in nearly 100,000 people in the United States ...

page 8 from 23