EU watchdog puts sickle cell disease drug on ice
The EU's drug watchdog Thursday called for the suspension of approval for Pfizer's medicine to treat sickle cell disease, saying doctors should stop using the drug.
Sep 26, 2024
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Congenital, Hereditary, and Neonatal Diseases and Abnormalities: News and Research on Anemia, Hemolytic, Congenital
MeSH tree: C16.320.070
Stroke rates increasing in individuals living with sickle cell disease despite treatment guidelines: Study
The incidence of stroke continues to increase for adults and children living with sickle cell disease (SCD), despite the Stroke Prevention Trial in Sickle Cell Anemia (STOP) establishing standards of care like transfusions ...
Sep 20, 2024
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Sickle cell trait is prevalent among diverse human populations, study finds
National Institutes of Health (NIH) researchers and collaborators have found that being a carrier for sickle cell disease, known as having sickle cell trait, increases the risk of blood clots, a risk that is the same among ...
Sep 12, 2024
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Sickle cell patients given Lactated Ringer's solution for pain improve more easily than those given normal saline
Sickle cell disease is a common genetic disorder characterized by periodic occurrences of pain that occur repeatedly throughout life. These episodes, referred to as vaso-occlusive episodes, happen when sickled cells obstruct ...
Sep 9, 2024
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Managing mental health is an important part of sickle cell disease treatment
Children who were diagnosed with a chronic condition at an early age face challenges that go beyond their physical health. Diseases like sickle cell have an especially stressful impact on not just the patient, but their families ...
Sep 9, 2024
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Cures for rare diseases now exist: Employers don't want to pay
As a wave of gene therapies with multimillion-dollar price tags hit the market, many employers are dropping coverage and leaving families in a bind.
Sep 9, 2024
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'Low-intensity' blood stem cell transplants for sickle cell appear safe for lung health
So-called low-intensity blood stem cell transplants, which use milder conditioning agents than standard stem cell transplants, do not appear to damage the lungs and may help improve lung function in some patients with sickle ...
Aug 27, 2024
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Editing fetal genomes is on the horizon—why ethical discussions with target communities should happen now
With their primary goal to advance scientific knowledge, most scientists are not trained or incentivized to think through the societal implications of the technologies they are developing. Even in genomic medicine, which ...
Aug 19, 2024
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Leading AI models struggle to identify genetic conditions from patient-written descriptions, researchers find
National Institutes of Health (NIH) researchers have discovered that while artificial intelligence (AI) tools can make accurate diagnoses from textbook-like descriptions of genetic diseases, the tools are significantly less ...
Aug 14, 2024
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CDC warns of resurgence of common respiratory virus, with risks for particular groups
Parvovirus B19, a seasonal respiratory virus that subsided during the pandemic, is making a comeback, U.S. health officials warned Tuesday.
Aug 14, 2024
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