Congenital, Hereditary, and Neonatal Diseases and Abnormalities: News and Research on Glycogen Storage Disease

MeSH tree: C16.320.565.202.449

New route into cells could make gene therapies safer

Scientists from the Centenary Institute and the University of Sydney have made a landmark discovery that could lead to safer and more effective gene therapies for a range of serious genetic disorders including Duchenne muscular ...