Congenital, Hereditary, and Neonatal Diseases and Abnormalities: News and Research on Walker-Warburg Syndrome

Using RNA interference to correct a mistake in the genetic code of patients with Fukuyama muscular dystrophy

Muscular dystrophy is a debilitating disease that causes progressive weakening and loss of muscles. Fukuyama congenital muscular dystrophy (FCMD), the second most common form of childhood muscular dystrophy in Japan, is a ...