Congenital, Hereditary, and Neonatal Diseases and Abnormalities: News and Research on X-Linked Combined Immunodeficiency Diseases

MeSH tree: C16.614.815.500

X-SCID gene therapy gives scientists a rare glimpse into early immune system

Findings from St. Jude Children's Research Hospital demonstrate that virtual memory T cells, a specialized group of immune cells, provide nonspecific immunity for infants early in life.

Jul 31, 2025

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3D genome architecture influences SCID-X1 gene therapy success

Patients with X-linked severe combined immunodeficiency disorder (SCID-X1), sometimes called "bubble boy disease," are born with a defective gene that prevents them from producing immune cells. Gene therapy from St. Jude ...

Oct 6, 2023

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