MeSH tree: C08.381.187
A systematic review of 52 scientific papers submitted to a world-leading clinical genetics journal from multiple scientists over a two-year period reveals that not a single one named critical gene mutations (correctly termed ...
Mar 9, 2026
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Engineers at the University of Pennsylvania and Rice University have refined a technology for editing individual genetic "base pairs" to a new level of precision, opening the door to safer, more reliable therapies for a wide ...
Feb 23, 2026
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In most states, Medicaid eligibility rules shift at age 19, when individuals transition from child to adult classification. A new study led by the University of Chicago finds that this policy threshold coincides with a sharp ...
Feb 19, 2026
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UCLA researchers have developed a lipid nanoparticle-based gene-editing approach capable of inserting an entire healthy gene into human airway cells, restoring key biological function in a laboratory model of cystic fibrosis ...
Feb 17, 2026
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Cystic fibrosis (CF) is the most common inherited metabolic disease in Europe. More than 8,000 people in Germany are affected. Every year, about 150 to 200 children are born with this incurable disease. It is caused by a ...
Feb 11, 2026
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When UNSW Associate Professor Shafagh Waters explains cystic fibrosis (CF) to the children she works with, she asks them to imagine what is happening inside their own bodies. "I tell them to picture an airport," she says. ...
Feb 6, 2026
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More children with medically complex conditions are surviving into adulthood, but researchers have had limited visibility into how these conditions influence adult hospital care. Young adults with complex chronic childhood-onset ...
Jan 28, 2026
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Artificial intelligence is increasingly used as a tool in many health care settings, from writing physicians' notes to making recommendations in specific cases. Research has found that AI and large language models can reflect ...
Jan 21, 2026
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Until relatively recently, children and young people with life-shortening conditions were not expected to survive into adulthood.
Jan 7, 2026
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A new multi-site study led by researchers at CU Anschutz shows that people with cystic fibrosis (CF) who start the triple-drug therapy elexacaftor/tezacaftor/ivacaftor (ETI) can safely reduce many of their daily lung treatments ...
Dec 5, 2025
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