Estrogen-related receptors could be key to treating metabolic and muscular disorders
A new Salk Institute study suggests that estrogen-related receptors could be a key to repairing energy metabolism and muscle fatigue.
May 12, 2025
0
29
Musculoskeletal Diseases: News and Research on Muscular Dystrophies
MeSH tree: C05.651.534.500
Dr. Vinay Prasad to head FDA vaccine, biologics division
The U.S. Food and Drug Administration (FDA) has chosen Dr. Vinay Prasad, a professor at the University of California-San Francisco, to lead its Center for Biologics Evaluation and Research.
May 7, 2025
0
14
Existing treatments may help fight symptoms of severe form of muscular dystrophy
A new study led by researchers at the Hospital for Special Surgery (HSS) suggests that currently available therapies may help control chronic muscle inflammation in Duchenne muscular dystrophy (DMD), a severe condition that ...
Apr 30, 2025
0
16
Rare diseases often go undiagnosed or untreated in parts of Africa. A project seeks to change that
Ndeye Lam visits the cemetery often, praying and gently touching the seashells laid out across her daughter's gravesite.
Apr 27, 2025
0
17
Setback in gene therapy for Duchenne muscular dystrophy as immune system emerges as key barrier
A new paper published in Gene Therapy raises serious concerns about the effectiveness of gene therapy for Duchenne muscular dystrophy (DMD), after the treatment failed to show significant benefit in a large-scale clinical ...
Apr 8, 2025
0
30
Many people with disabilities risk losing their Medicaid if they work too much
Zach Mecham has heard politicians demand that Medicaid recipients work or lose their benefits. He has also run into a jumble of Medicaid rules that effectively prevent many people with disabilities from holding full-time ...
Mar 31, 2025
0
12
Duchenne muscular dystrophy's impact on the brain may be reversible
New research led by the University of Portsmouth has revealed how Duchenne muscular dystrophy (DMD), best known for causing severe muscle degeneration, also profoundly affects the brain, leading to cognitive and behavioral ...
Mar 28, 2025
0
26
New protein target identified for muscle repair and regeneration
For millions of people, losing muscle isn't just about weakness; it's about losing independence. Whether caused by Duchenne muscular dystrophy, aging or other degenerative conditions, muscle loss can make everyday activities—like ...
Mar 26, 2025
0
48
Sarepta's gene therapy under scrutiny after patient death
A patient has died while receiving Elevidys, a gene therapy for Duchenne muscular dystrophy, marking the first known death linked to the treatment.
Mar 19, 2025
0
24
Patient dies following muscular dystrophy gene therapy, Sarepta reports
Sarepta Therapeutics said Tuesday that a patient died while taking its closely watched gene therapy for muscular dystrophy, sending company shares plummeting more than 25%.
Mar 18, 2025
0
17
