MeSH tree: C10.668.491.175.500.300
A cell therapy called deramiocel could slow muscle weakening in boys and young men with advanced Duchenne muscular dystrophy (DMD) and may also slow heart damage in those who already have heart muscle disease, a Phase III ...
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Researchers at the USF Health Morsani College of Medicine have identified a potential pathway that could protect cardiac function in people with Duchenne muscular dystrophy (DMD), a progressive and fatal genetic disease that ...
Jul 17, 2026
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At Binghamton University, researchers were among the first to find ways to help patients with Duchenne muscular dystrophy (DMD) through the development of an effective drug. Now, they are continuing that work, looking to ...
Jun 30, 2026
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A new treatment platform developed by researchers at the University of Texas MD Anderson Cancer Center was able to deliver messenger RNA (mRNA) of the full-length DMD gene into preclinical models of Duchenne muscular dystrophy, ...
Jun 11, 2026
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Rare neuromuscular diseases often lack treatments because developing targeted drugs is slow, costly and risky for companies. A new approach using AI and stem cell models could finally shift the balance.
May 12, 2026
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When stem cells are injected into thick tissues, they often clump together and die from lack of oxygen or nutrients, making it almost impossible to use them for thick, highly vascularized tissues like organ transplants or ...
Mar 23, 2026
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A preclinical study led by the Germans Trias i Pujol Research Institute (IGTP), in collaboration with the Institut de Myologie and the Sant Pau Research Institute, has analyzed the role of the protein HDAC11 in Duchenne muscular ...
Feb 9, 2026
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In research published in Developmental Medicine & Child Neurology, investigators have developed a brief, reliable, and valid screening tool to help identify individuals with Duchenne muscular dystrophy (a neuromuscular disorder) ...
Jan 14, 2026
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Until relatively recently, children and young people with life-shortening conditions were not expected to survive into adulthood.
Jan 7, 2026
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The United States on Friday said it would add its most serious warning label to a gene therapy treatment for a debilitating muscle-wasting disease, and also limit its approved use.
Nov 15, 2025
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