MeSH tree: E04.936.225.687.500
Australian researchers have demonstrated that the use of a new, less toxic drug combination after stem cell transplants for leukemia significantly improves patient outcomes post-transplant, reducing the risk of the life-threatening ...
Jun 16, 2025
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A Kennedy Krieger Institute researcher is playing a role in a major international effort that has yielded a promising first-ever drug treatment for cerebral adrenoleukodystrophy (cALD)—a rare, often fatal genetic brain disease ...
Jun 2, 2025
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A collaborative team of researchers from Children's Hospital of Philadelphia (CHOP) found that hematopoietic stem cell transplantation (HSCT) is a highly effective method for treating patients with monogenic inflammatory ...
May 21, 2025
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An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life-threatening immune disorder called severe leukocyte adhesion deficiency-I, or LAD-I, in an international ...
Apr 30, 2025
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A research team has identified the impact of stem cell infusion timing on the incidence and severity of acute graft-versus-host disease (aGVHD) in allogeneic hematopoietic stem cell transplantation (allo-HSCT), highlighting ...
Mar 31, 2025
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Our blood consists of many cell types that develop through different stages from a precursor type—the blood stem cell. An international research team led by Universitätsmedizin Frankfurt and Goethe University has now investigated ...
Mar 21, 2025
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In a preclinical study, researchers at Children's Hospital of Philadelphia (CHOP) demonstrated a novel gene therapy with potentially increased effectiveness and safety for the treatment of metachromatic leukodystrophy (MLD), ...
Mar 12, 2025
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Right now, approximately 20 billion red blood cells are busy traveling through your blood vessels. They are delivering oxygen to all the different tissues in your body and removing carbon dioxide to be breathed out of your ...
Feb 10, 2025
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In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches—gene therapy and bone marrow transplantation—to alleviate symptoms of multiple sulfatase deficiency (MSD), an ultra-rare ...
Jan 29, 2025
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In a room at Maisonneuve-Rosemont Hospital in Montreal, a patient puts on a virtual reality (VR) headset. Bright bubbles float slowly up and down before his eyes while soothing sounds play in the background.
Jan 22, 2025
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