We have drugs to manage HIV. So why are we spending millions looking for cures?
Over the past three decades, there have been amazing advances in treating and preventing HIV.
Jul 1, 2025
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Surgical Procedures, Operative: News and Research on Hematopoietic Stem Cell Transplantation
MeSH tree: E04.936.225.687.500
New development in stem cell transplant for blood cancers set to change 40 years of standard practice
Australian researchers have demonstrated that the use of a new, less toxic drug combination after stem cell transplants for leukemia significantly improves patient outcomes post-transplant, reducing the risk of the life-threatening ...
Jun 16, 2025
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Oral drug shows promise for slowing fatal childhood brain disease
A Kennedy Krieger Institute researcher is playing a role in a major international effort that has yielded a promising first-ever drug treatment for cerebral adrenoleukodystrophy (cALD)—a rare, often fatal genetic brain disease ...
Jun 2, 2025
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Stem cell transplant offers potentially curative therapy in pediatric patients with monogenic inflammatory bowel disease
A collaborative team of researchers from Children's Hospital of Philadelphia (CHOP) found that hematopoietic stem cell transplantation (HSCT) is a highly effective method for treating patients with monogenic inflammatory ...
May 21, 2025
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Investigational gene therapy gives children with rare immune disorder a new lease on life
An investigational gene therapy has successfully restored immune function in all nine children treated with the rare and life-threatening immune disorder called severe leukocyte adhesion deficiency-I, or LAD-I, in an international ...
Apr 30, 2025
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Stem cell infusion timing can prevent acute graft-versus-host disease
A research team has identified the impact of stem cell infusion timing on the incidence and severity of acute graft-versus-host disease (aGVHD) in allogeneic hematopoietic stem cell transplantation (allo-HSCT), highlighting ...
Mar 31, 2025
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How stem cells calm the body's immune response
Our blood consists of many cell types that develop through different stages from a precursor type—the blood stem cell. An international research team led by Universitätsmedizin Frankfurt and Goethe University has now investigated ...
Mar 21, 2025
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Preclinical study demonstrates improved gene therapy approach to treating a rare and devastating disease in children
In a preclinical study, researchers at Children's Hospital of Philadelphia (CHOP) demonstrated a novel gene therapy with potentially increased effectiveness and safety for the treatment of metachromatic leukodystrophy (MLD), ...
Mar 12, 2025
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Sickle cell disease is a genetic disorder that causes lifelong suffering—here's what you need to know
Right now, approximately 20 billion red blood cells are busy traveling through your blood vessels. They are delivering oxygen to all the different tissues in your body and removing carbon dioxide to be breathed out of your ...
Feb 10, 2025
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Gene therapy and bone marrow transplant alleviate ultra-rare genetic disease symptoms
In two new papers, researchers from The Jackson Laboratory (JAX) report the successful use of two approaches—gene therapy and bone marrow transplantation—to alleviate symptoms of multiple sulfatase deficiency (MSD), an ultra-rare ...
Jan 29, 2025
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