Enzyme therapy shows promise for childhood dementia
Studies into a rare nervous system disorder that causes dementia and early death in children have highlighted a possible treatment for the condition.
Oct 11, 2022
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Therapeutics: News and Research on Enzyme Therapy
MeSH tree: E02.319.353
FDA approves first treatment for acid sphingomyelinase deficiency
The U.S. Food and Drug Administration has approved Xenpozyme (olipudase alfa) for pediatric and adult patients with acid sphingomyelinase deficiency (ASMD), a rare genetic disease.
Sep 5, 2022
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