First patients dosed with 'gene silencing' drug for Huntington's disease
The first few patients have received doses of an experimental RNA-targeting drug for Huntington's disease, it was announced today.
Oct 19, 2015
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The first few patients have received doses of an experimental RNA-targeting drug for Huntington's disease, it was announced today.
Oct 19, 2015
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A new DNA test, developed by researchers at the Garvan Institute of Medical Research in Sydney and collaborators from Australia, UK and Israel, has been shown to identify a range of hard-to-diagnose neurological and neuromuscular ...
Mar 4, 2022
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A drug already used to treat certain forms of cancer may also be an effective therapy for Huntington's disease, according to a new study in the latest issue of Science Translational Medicine. The same study also increases ...
Dec 6, 2017
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Treatment that increases brain levels of an important regulatory enzyme may slow the loss of brain cells that characterizes Huntington's disease (HD) and other neurodegenerative disorders. In a report receiving advance online ...
Dec 18, 2011
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Huntington's, Alzheimer's, ALS, and multiple other neurodegenerative diseases share a commonality: They are all characterized by proteins (different ones for each disease) aggregating in neurons within the brain and nervous ...
Feb 16, 2022
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A new variant of the gene-editing CRISPR/Cas9 system is safer and more specific than versions previously used in early research towards a treatment for Huntington's disease, shows research published today in Frontiers in ...
Feb 26, 2018
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A new scientific study reveals one way to stop proteins from triggering an energy failure inside nerve cells during Huntington's disease. Huntington's disease is an inherited genetic disorder caused by mutations in the gene ...
Sep 13, 2016
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The protein that is mutated in Huntington's disease is critical for wiring the brain in early life, according to a new Duke University study.
Jul 8, 2014
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"It came completely out of the blue," says James*. They had thought it was his father's knees that were the problem – he was never comfortable and was constantly shifting them. "He went to the doctor, and he said, 'You ...
Mar 6, 2018
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Patients with Huntington's disease, a fatal genetic illness that causes the breakdown of nerve cells in the brain, have up to 80 percent less cancer than the general population.
Feb 12, 2018
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