MeSH tree: C16.320.365.826.150
After approving Casgevy (exagamglogene autotemcel) in December to treat sickle cell disease, the U.S. Food and Drug Administration announced Tuesday that the therapy has now been approved to treat patients older than 12 years ...
Jan 17, 2024
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Lyric Porter wanted her life back. Born with sickle cell disease, she had a fever at age 5 that scarred her lungs and required her to roll an oxygen tank to school. When she was growing up, clogged blood vessels racked her ...
Jan 3, 2024
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A Cambridge-led study has shown why many women experience nausea and vomiting during pregnancy—and why some women, including the Duchess of Cambridge, become so sick they need to be admitted to hospital.
Dec 13, 2023
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This article includes an interview with Dr. Androulla Eleftheriou, Executive Director at TIF, and Dr. Zhiyu Peng, Deputy GM at BGI Genomics, Head of the World Hemoglobinopathy Foundation
Dec 4, 2023
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The gene-editing technology CRISPR shows early promise as a therapeutic strategy for the aggressive and difficult-to-treat brain cancer known as primary glioblastoma, according to findings of a new study from Gladstone Institutes.
Nov 27, 2023
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Researchers from multiple institutions in China have found a way to use gene editing to reactivate dormant fetal oxygen-transporting proteins in adult blood cells to potentially reverse a wide range of blood disorders.
Born with a deadly blood disease, Clint and Alissa Finlayson's adopted daughters—Ada, nine, and Lily, 12—are the first patients on the West Coast to receive a new gene therapy offered by UCSF Benioff Children's Hospital Oakland.
Oct 28, 2023
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Around 5.2% of the global population carries abnormal hemoglobin genes. Each year, 300,000 to 500,000 children are born with severe hemoglobinopathies worldwide, with approximately 80% of these cases occurring in developing ...
Sep 4, 2023
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UCSF Benioff Children's Hospital Oakland is the first hospital in the West to administer a newly approved gene therapy to treat beta thalassemia, a rare, genetic blood disorder that causes severe anemia, with a need for lifelong ...
Aug 31, 2023
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ETH Zurich molecular biologist Mandy Boontanrart is researching gene therapies that could be used to cure two of the most common types of inherited anemia. She has now developed a promising approach for so-called beta-hemoglobinopathies. ...
Aug 2, 2023
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